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EMICIZUMAB DATA

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Publications

Select publications and scientific data presentations with the strongest and most relevant data are provided below.

Bone and Joint Health

Bone and Joint Health Markers in Persons With Hemophilia A (PwHA) Treated With Emicizumab in the HAVEN 3 Clinical Trial

Kiialaninen A, Castaman G, Chang T, et al. Presented at the Virtual NHF Scientific Meeting; August 1-8, 2020. 

Healthcare Costs and Value

[RECENTLY ADDED] Valoctocogene Roxaparvovec and Emicizumab for Hemophilia A Without Inhibitors: Effectiveness and Value (Report-at-a-Glance)

Institute for Clinical and Economic Review, 2020

Hemophilia A and Mortality

[RECENTLY ADDED] Mortality in Congenital Hemophilia A - A Systematic Literature Review

Hay CRM, Nissen F, and Pipe SW. J Thromb Haemost 2020;DOI: 10.1111/jth.15189

[RECENTLY ADDED] Establishment of a Framework for Assessing Mortality in Persons With Congenital Hemophilia A and its Application to an Adverse Event Reporting Database

Pipe SW, Kruse-Jarres R, Mahlangu JN, et al. J Thromb Haemost 2020; DOI: 10.1111/jth.15186

[RECENTLY ADDED] Application of a Hemophilia Mortality Framework to the Emicizumab Global Safety Database

Peyvandi F, Mahlangu JN, Pipe SW, et al. J Thromb Haemost 2020; DOI: 10.1111/jth.15187

A Systematic Review of Mortality Statistics and Causes of Death in People With Congenital Hemophilia A (PwcHA)

Hay C, Nissen F, and Pipe S. Presented at the Virtual NHF Scientific Meeting; August 1-8, 2020.

A Contemporary Framework For Understanding Mortality in People With Congenital Hemophilia A (PwcHA)

Pipe S, Kruse-Jarres R, Mahlangu J, et al. Presented at the Virtual NHF Scientific Meeting; August 1-8, 2020. 

An Analysis of Fatalities in Persons With Congenital Hemophilia A Reported in the FDA Adverse Event Reporting System (FAERS) Database

De Ford C, Kuebler P, Shang A, et al. Presented at the Virtual NHF Scientific Meeting: August 1-8, 2020.

Impact of Inhibitors on Hemophilia A Mortality in the United States

Walsh CE, Soucie JM, Miller CH, et al. Am J Hematol. 2015;90:400–405.

Real-World Experience

 Emicizumab Treatment and Monitoring in a Paediatric Cohort: Real-World Data

Barg AA, Livnat T, Budnik I,  et al. Br J Haematol. 2020; DOI: 10.1111/bjh.16964. 

Real-World Use of Emicizumab in Patients With Haemophilia A: Bleeding Outcomes and Surgical Procedures

McCary I, Guelcher C, Kuhn J, et al. Haemophilia. 2020;26:631636.

Emicizumab Prophylaxis in Patients With Haemophilia A With and Without Inhibitors

Ebbert PT, Xavier F, Seaman D, et al. Haemophilia. 2020;26:41–46.

Emicizumab Prophylaxis Among Infants and Toddlers With Severe Hemophilia A and Inhibitors-a Single-Center Cohort

Barg AA, Avishai E, Budnik I, et al. Pediatr Blood Cancer. 2019;66:e27886.